Official Title
Post-trial Access Program: Idursulfase-IT (HGT-2310) in Conjunction With Intravenous Elaprase® in Pediatric and Adult Patients With Hunter Syndrome and Cognitive Impairment
Brief Summary

As the HGT-HIT-046 (NCT01506141) and SHP609-302 (NCT02412787) studies will be closed,this post-trial access (PTA) program provides TAK-609 to participants in these studiesfor whom the benefit:risk ratio of continued treatment with idursulfase-IT remainspositive.

Detailed Description

Not Provided

Available
Intermediate-size Population
Hunter Syndrome

Drug: Idursulfase-IT

Participants will continue to receive the same dose of idursulfase-IT, once monthly, that
was administered during the HGT-HIT-046 [NCT01506141] or SHP609-302 [NCT02412787] study
[10mg or 30mg] along with intravenous (IV) infusions of standard-of-care therapy Elaprase
via intrathecal drug delivery device (IDDD) or lumbar punctures.
Other Name: HGT-2310,TAK-609

Eligibility Criteria

Inclusion Criteria:

1. Participants will have completed the treatment period of the HGT-HIT-046
(NCT01506141) or SHP609-302 (NCT02412787) study prior to the first dose on this
program.

2. Participant and/or a parent(s)/legal guardian is informed of the nature of this
compassionate post-trial access program and can provide written informed consent for
themselves or the child to participate (with assent from the child when appropriate
prior to treatment).

Exclusion Criteria:

1. Participant has a condition that in the opinion of the treating physician may
compromise their safety.

2. Participant has a known hypersensitivity to idursulfase-IT or its components.

Eligibility Gender
Male
Eligibility Age
Minimum: N/A ~ Maximum: N/A
Countries
Australia
Mexico
Spain
United Kingdom
United States
Locations

Phoenix Childrens Hospital
Phoenix 5308655, Arizona 5551752, United States

The Regents of the University of California
Oakland 5378538, California 5332921, United States

The Nemours Foundation
Wilmington 4145381, Delaware 4142224, United States

Jackson Memorial Hospital University of Miami
Miami 4164138, Florida 4155751, United States

Ann and Robert H Lurie Childrens Hospital of Chicago
Chicago 4887398, Illinois 4896861, United States

Washington University
Washington 4413621, Missouri 4398678, United States

Board of Regents of the University of Nebraska
Omaha 5074472, Nebraska 5073708, United States

Joseph M. Sanzari Children's Hospital
Hackensack 5098706, New Jersey 5101760, United States

NYU Langone Medical Center
New York 5128581, New York 5128638, United States

The University of North Carolina
Chapel Hill 4460162, North Carolina 4482348, United States

The Cleveland Clinic Foundation
Cleveland 5150529, Ohio 5165418, United States

Randall Children's Hospital at Legacy Emanuel
Portland 5746545, Oregon 5744337, United States

The Children's Hospital of Philadelphia
Philadelphia 4560349, Pennsylvania 6254927, United States

UPMC Childrens Hospital of Pittsburgh
Pittsburgh 5206379, Pennsylvania 6254927, United States

Vanderbilt Children's Hospital
Nashville 4644585, Tennessee 4662168, United States

Division of Medical Genetics, University of Utah
Salt Lake City 5780993, Utah 5549030, United States

Seattle Children's Hospital - PIN
Seattle 5809844, Washington 5815135, United States

Queensland Childrens Hospital
South Brisbane 2207259, Queensland 2152274, Australia

Instituto Nacional de Pediatria
Coyoacán 3530139, Mexico City 3527646, Mexico

H.C.U. de Valladolid
Valladolid 3514876, Mexico

Hospital Universitario Reina Sofia
Córdoba 2519240, Spain

Royal Manchester Children's Hospital - PPDS
Manchester 2643123, United Kingdom

Contacts

Takeda Contact
+1877-825-3327
medinfoUS@takeda.com

Study Director, Study Director
Takeda

NCT Number
MeSH Terms
Mucopolysaccharidosis II