Official Title
An Expanded Access Protocol for the Treatment of Glioblastoma Multiforme in Patients With Already Manufactured DCVax®-L, Autologous Dendritic Cells Pulsed With Tumor Lysate Antigen Who Have Screen-Failed Protocol 020221
Brief Summary

The study is an open-label expanded access study for patients for whom vaccine wasmanufactured during the Northwest Biotherapeutics' 020221 DCVax-L for GBM screeningprocess, but who subsequently failed to meet specific enrollment criteria. Patients willreceive therapy per investigator discretion (standard of care) as well as active vaccineper the 020221 protocol administration schedule. It is estimated that approximately 99patients will enroll in this study.

Detailed Description

Patients who are being screened under protocol 020221 who are not eligible for enrollment
due to a) evidence of disease progression or pseudo-progression post chemo-radiation or
b) insufficient (<5 doses) vaccine manufactured, and for whom the DCVax-L treatment was
manufactured and released are eligible for this study.

Treatment Schedule:

Open label vaccine injections will be give per the associated 020221 protocol. Injections
will be given at days 0, 10, 20, and at months 2, 4, 8, 12, 18, 24 and 30. There are no
therapeutic restrictions, but guidelines for drug administration are recommended as per
the 020221 protocol.

Data collected includes vaccine administration information, and any vaccine related
adverse event. Patient MRIs will be collected centrally for future review. Patients will
be followed for disease progression and survival.

Available
GBM
Glioblastoma Multiforme

Biological: DCVax-L

Autologous Dendritic Cells Pulsed with Tumor Lysate Antigen

Eligibility Criteria

Inclusion Criteria:

1. Screen-Fail for protocol 020221 due to either:

- Radiographic evidence of disease progression or pseudoprogression at the
Baseline visit under protocol 020221, as determined by central imaging review,
OR

- Insufficient vaccine manufactured for protocol 020221 (i.e. less than 5 doses).

2. Patients must have a KPS rating of ≥70 at the Baseline Visit (Visit 5) (refer to
Appendix D, Performance Status Scales).

3. Patients may have received steroid therapy as part of their primary treatment.
Steroid treatment should preferably be stopped; or if continued steroid use is
clinically indicated, be tapered down to no more than 4 mg dexamethasone qd at least
7 days prior to the first immunization .

4. DCVax-L product manufactured and released.

Exclusion Criteria:

1. Active uncontrolled infection, or acute infection requiring antibiotic or antifungal
therapy. Antibiotic and antifungal therapy should be completed approximately 7 days
prior to the first immunization.

2. Fever ≥101.5oF. If considered possibly transient, retesting is allowed.

3. Unstable or severe intercurrent medical conditions.

4. Females of child-bearing potential who are pregnant or lactating or who are not
using adequate contraception (abstinence, surgical, hormonal or double barrier, i.e.
condom and diaphragm). 020221 Baseline lab results and or local lab results are
acceptable.

Eligibility Gender
All
Eligibility Age
Minimum: 18 Years ~ Maximum: 70 Years
Countries
United States
Locations

University of Arkansas for Medical Sciences
Little Rock 4119403, Arkansas 4099753, United States

UCLA Medical Center
Los Angeles 5368361, California 5332921, United States

Hoag Memorial Hospital
Newport Beach 5376890, California 5332921, United States

St. Joseph Hospital of Orange
Orange 5379513, California 5332921, United States

University of California, Irvine Medical Center
Orange 5379513, California 5332921, United States

University of Colorado Cancer Center
Aurora 5412347, Colorado 5417618, United States

Colorado Neurological Institute
Englewood 5421250, Colorado 5417618, United States

University of Florida
Gainesville 4156404, Florida 4155751, United States

Memorial Healthcare System Memorial Cancer Institute
Hollywood 4158928, Florida 4155751, United States

Cadence Cancer Center at Warrenville
Warrenville 4915525, Illinois 4896861, United States

Beth Israel Deaconess Medical Center
Boston 4930956, Massachusetts 6254926, United States

Spectrum Health
Grand Rapids 4994358, Michigan 5001836, United States

John Nasseff Neuroscience Institute - Abott Northwestern Hospital
Minneapolis 5037649, Minnesota 5037779, United States

Saint Luke's Hospital of Kansas City
Kansas City 4393217, Missouri 4398678, United States

Washington University School of Medicine
St Louis 4407066, Missouri 4398678, United States

John Theurer Cancer Center at Hackensack University Medical Center
Hackensack 5098706, New Jersey 5101760, United States

Capital Health
Trenton 5105496, New Jersey 5101760, United States

North Shore University Hospital
Manhasset 5125766, New York 5128638, United States

Columbia University Medical Center Neurological Institute of New York
New York 5128581, New York 5128638, United States

Stony Brook University Hospital
Stony Brook 5139865, New York 5128638, United States

Ohio State University
Columbus 4509177, Ohio 5165418, United States

University of Oklahoma Health Science Center
Oklahoma City 4544349, Oklahoma 4544379, United States

Geisinger Medical Center
Danville 5186327, Pennsylvania 6254927, United States

Hospital of the University of Pennsylvania
Philadelphia 4560349, Pennsylvania 6254927, United States

Saint Thomas Research Institute
Nashville 4644585, Tennessee 4662168, United States

Swedish Neuroscience Institute
Seattle 5809844, Washington 5815135, United States

Aurora Saint Luke's Medical Center
Milwaukee 5263045, Wisconsin 5279468, United States

Contacts

Marnix Bosch, MBA PhD
240 497 9022
marnix@nwbio.com

Meghan Swardstrom
425 492 6036
mswardstrom@nwbio.com

Northwest Biotherapeutics
NCT Number
Keywords
GBM
Brain tumor
glioblastoma
Brain tumor WHO grade IV
MeSH Terms
Glioblastoma
Brain Neoplasms