Official Title
Compassionate Use for BIA 28-6156 in Patients With Parkinson's Disease (PD) Who Have a Pathogenic Variant in the GBA1 Gene (GBA-PD) and Completed the ACTIVATE Study
Brief Summary

This Program is designed to provide continued access BIA 28-6156, free andcompassionately for an eligible patient previously enrolled in the BIA 28-6156-201(ACTIVATE) clinical study and that had completed the study.

Detailed Description

A patient taking part in this program will be provided with a 60mg dosage of BIA 28-6156.
This will be taken orally once daily (OD) for the duration of the program, currently
scheduled to run for 27 months.

Patients will visit the site approximately every 3 months for a drug re-supply. At these
visits, the treating physician will reassess if the patient should continue with the
treatment.

In case of tolerability concerns, the dose of BIA 28-6156 will be stopped per the
treating physician's assessment.

The treating physician should discontinue treatment for the patient and/or withdraw the
patient from this program if he/she believes that continuation would be detrimental to
the patient's well-being.

Patients may voluntarily withdraw from treatment at any time, for any reason.

Available
Treatment IND/Protocol
Parkinson Disease

Drug: BIA 28-6156

60mg dosage of BIA 28-6156 taken orally once daily

Eligibility Criteria

Inclusion Criteria:

1. A patient who completes Part B (Double Blind Treatment arm) of the ACTIVATE study
supplied by BIAL R&D Investments, S.A., and falls within one week of completing the
safety follow up visit from the ACTIVATE study.

2. A patient is willing to provide written informed consent prior to initiating
treatment, in accordance with International Conference on Harmonization (ICH) Good
Clinical Practice (GCP) guidelines. A patient who, in the opinion of the treating
physician will likely adhere to the program.

3. A patient's treating physician believes the patient could benefit from treatment
with BIA 28-6156.

4. Patient has received approval from Supplier or its designee following the treating
physician request submission.

5. If a sexually active man or a woman of childbearing potential, the patient agrees to
use highly effective birth control or to remain abstinent during the program and for
30 days after the last dose of BIA 28-6156. Acceptable (highly effective) methods of
contraception for this study include hormonal contraceptives (combined oral
contraceptive, patch, vaginal ring, injectable, or implant); intrauterine device or
system; complete abstinence from sexual intercourse if this is the patient's usual
and preferred lifestyle; or sexual partner with surgical sterilization (e.g., tubal
ligation, hysterectomy and/or bilateral oophorectomy.

Exclusion Criteria:

1. A patient that has previously discontinued for any reason from the BIA 28-6156-201
clinical study.

2. A patient who is pregnant, may be pregnant, lactating, or planning to be pregnant.

Eligibility Gender
All
Eligibility Age
Minimum: N/A ~ Maximum: N/A
Countries
Italy
Portugal
Spain
United Kingdom
United States
Locations

Barrow Neurological Institute
Phoenix, Arizona, United States

University of Colorado
Aurora, Colorado, United States

Parkinson's Center and Movement Disorders of Boca Raton
Boca Raton, Florida, United States

University of Miami, Dept. of Neurology
Miami, Florida, United States

Northwestern University
Chicago, Illinois, United States

University of Kansas Medical Center
Kansas City, Kansas, United States

University of Kentucky
Lexington, Kentucky, United States

University of Maryland Medical Center
Baltimore, Maryland, United States

Massachusetts General Hospital
Boston, Massachusetts, United States

Park Nicollet Struther's Parkinson's Center (Struthers Parkinsons Center at HealthPartners)
Saint Paul, Minnesota, United States

Cleveland Clinic Foundation
Cleveland, Ohio, United States

MUSC
Charleston, South Carolina, United States

Vanderbilt Medical Center
Nashville, Tennessee, United States

Intermountain Healthcare
Salt Lake City, Utah, United States

University of Washington
Seattle, Washington, United States

Inland Northwest Research
Spokane, Washington, United States

IRCCS Istituto Delle Scienze Neurologiche DI
Bologna, Italy

Spedali Civilia di Brescia
Brescia, Italy

Ospedale Antonio Perrino
Brindisi, Italy

Fondazione IRCCS Ca Granda Ospedale Maggiore Policlinico
Milan, Italy

Universita degli Studi della Campania Luigi Vanvitelli - Clinica Neurologia I
Naples, Italy

Universita degli Studi di Padova - Azienda Ospedaliera di Padova - Clinica Neurologica
Padova, Italy

IRCSS San Raffaele Pisana
Roma, Italy

A.O.U. San Giovanni di Dio Ruggi d'Aragona Centro Parkinson- Piano Rialzato Corpo QT
Salerno, Italy

Hospital Senhora da Oliveira de Guimaraes
Guimarães, Portugal

Hospital Universitari Germans Trias i Pujol
Badalona, Spain

Hospital Universitario Cruces
Barakaldo, Spain

Hospital de la Santa Creu I Sant Pau
Barcelona, Spain

Hospital Vall D´Hebron
Barcelona, Spain

Hospital Universitaio de La Princesa
Madrid, Spain

Hospital Ruber Internacional
Madrid, Spain

Hospital Universitario Virgen del Rocio
Seville, Spain

NHS Tayside-Ninewells Hospital and Medical School
Dundee, United Kingdom

King's College London - David Goldberg Centre
London, United Kingdom

The Newcastle upon Tyne Hospitals NHS Foundation Trust, Freeman Hospital
Newcastle upon Tyne, United Kingdom

University Hospitals Plymouth NHS Trust
Plymouth, United Kingdom

Contacts

Raquel Costa
00351229866100
raquel.costa@bial.com

Miguel Fonseca
00351229866100
miguel.fonseca@bial.com

Not Provided

Bial R&D Investments, S.A.
NCT Number
Keywords
Parkinson's Disease
Neurodegenerative Diseases
Central Nervous System Diseases
Parkinsonian Disorders
movement disorders
GBA1 gene
BIA 28-6156
ACTIVATE
Compassionate Use
MeSH Terms
Parkinson Disease
Neurodegenerative Diseases
Central Nervous System Diseases
Parkinsonian Disorders
Movement Disorders