Official Title
A Phase 1, Open-Label, First-in-Human, Dose Escalation Study to Investigate the Safety, Pharmacokinetics, Pharmacodynamics and Preliminary Efficacy of MT-303 in Adults With Advanced or Metastatic GPC3-Expressing Cancers, Including Hepatocellular Carcinoma
Brief Summary

This is a multicenter, open-label, Phase 1, first-in-human, dose-escalation studydesigned to assess the safety, tolerability and define the RP2D of MT-303 in participantswith advanced hepatocellular carcinoma expressing GPC3.

Detailed Description

MT-303 will be administered intravenously with treatment provided until lack of
tolerability or progression. Participants will be enrolled in sequential dose escalation
cohorts with determination of dose limiting toxicities with the goal of establishing the
(maximum tolerated dose) MTD and (Recommended Phase 2 dose) RP2D.

Recruiting
HepatoCellular Carcinoma

Drug: MT-303

MT-303

Eligibility Criteria

Inclusion Criteria

- Aged 18 years or older

- Histological diagnosis of advanced/recurrent or metastatic and/or unresectable HCC.
[Note: participants with other tumor types expressing GPC3 may be eligible pending a
discussion with the Medical Monitor]

- Measurable lesion per RECIST 1.1 criteria

- Eastern Cooperative Oncology Group (ECOG) performance status grade of 0 or 1

- Child-Pugh score: Class A

- Adequate organ function

Exclusion Criteria

- Known active central nervous system (CNS) metastasis and/or carcinomatous
meningitis.

- Any acute illness including active infection

- History of liver transplantation or on waiting list

- Participants with untreated or incompletely treated varices with bleeding or high
risk for bleeding

- Uncontrolled pleural effusion, pericardial effusion, or ascites

- History of symptomatic congestive heart failure

- History of chronic or recurrent (within the last year) severe autoimmune or immune
mediated disease requiring steroids or other immune-suppressive treatments.

Eligibility Gender
All
Eligibility Age
Minimum: 18 Years ~ Maximum: N/A
Countries
Australia
South Korea
Locations

St Vincent's Hospital
Sydney 2147714, New South Wales 2155400, Australia

Integrated Clinical Oncology Network (ICON) Pty Ltd
Woolloongabba 6943568, Queensland 2152274, Australia

The Alfred Hospital
Melbourne 2158177, Victoria 2145234, Australia

Linear Clinical Research
Murdoch 8349091, Western Australia 2058645, Australia

Pusan National Univesity Hospital
Busan 1838524, South Korea

Cha University Bundang Medical Center
Gyeonggi-do 6363696, South Korea

Seoul National University Hospital
Seoul 1835848, South Korea

Contacts

Project Manager
+61 2 8569 1400
Lucy.FrereScott@novotech-cro.com

Clinical Department
+1 617 465 1022
303clinical@myeloidtx.com

Matthew Maurer, MD, Study Director
Myeloid Therapeutics

Myeloid Therapeutics
NCT Number
Keywords
liver cancer
Hepatocellular carcinoma (HCC)
Glypican-3
Chimeric antigen receptor
CAR-M
MeSH Terms
Carcinoma, Hepatocellular
Liver Neoplasms
Simpson-Golabi-Behmel syndrome