Brief Summary
Individual patient expanded access requests may be considered for patients who have no other treatment options
Detailed Description
Expanded access may be available outside of the US in countries prior to approval by the
local regulatory agencies. For full details, please visit the links provided below.
Available
Individual Patients
MPS VII
Mucopolysaccharidosis VII
Sly Syndrome
Drug: Mepsevii
Other Name: Array
Eligibility Criteria
Inclusion Criteria:
-
Exclusion Criteria:
-
Eligibility Gender
All
Eligibility Age
Minimum: N/A ~ Maximum: N/A
Contacts
Early Access
1-415-483-8800
EarlyAccess@ultragenyx.com
Ultragenyx Pharmaceutical Inc
NCT Number
Keywords
Expanded Access
Compassionate Use
MeSH Terms
Mucopolysaccharidoses
Mucopolysaccharidosis VII